News & Reports

Ultragenyx Announces Positive Interim Phase 1/2 Data in Patients with Angelman Syndrome After Treatment with GTX-102
NBLC News Joanne Webster NBLC News Joanne Webster

Ultragenyx Announces Positive Interim Phase 1/2 Data in Patients with Angelman Syndrome After Treatment with GTX-102

Ultragenyx reveals promising interim Phase 1/2 data showing rapid, multi-domain improvements in patients with Angelman syndrome treated with GTX-102, offering new hope for a disease that currently lacks any approved treatment—find out more about these groundbreaking results and what’s next in their development.

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